From mind-controlling tech to clinical therapy: An optogenetics roadmap

Researchers at the University of Geneva, together with colleagues in Switzerland, France, the United States and Israel, ...
Science Daily

Gene-edited CAR-T cells erase aggressive T-cell leukemia

A cutting-edge therapy using base-edited immune cells is offering a major breakthrough for patients with one of the toughest ...
Kalkine Media

Sarepta Therapeutics (NASDAQ:SRPT) Nasdaq Index Tracks Biotech Advancements

Sarepta Therapeutics (NASDAQ:SRPT) leads in genetic therapies, contributing to ongoing discussions surrounding the nasdaq ...
BioSpace

FDA Greenlights First Gene Therapy for Rare Pediatric Disease

Backed by Italy-based Fondazione Telethon ETS, Waskyra, for Wiskott-Aldrich syndrome, is the first gene therapy from a ...
Kalkine Media

Rocket Pharmaceuticals (NASDAQ:RCKT) Nasdaq Index Drives Rare-Disease Research

Rocket Pharmaceuticals (NASDAQ:RCKT) advances gene-therapy innovation and appears in broader discussions involving the nasdaq ...

Gene therapy improves movement in kids with spinal muscular atrophy

A single-dose gene replacement therapy is found to improve movement ability in children over 2 years of age and teenagers with spinal muscular atrophy, according to research published in Nature ...