The National Institute for Health and Care Excellence (NICE) has approved vamorolone (Agamree, Santhera) as a treatment option for Duchenne muscular dystrophy (DMD) following a revised pricing deal ...
The FDA has approved the addition of a Boxed Warning and other labeling changes for the Duchenne muscular dystrophy (DMD) gene therapy delandistrogene moxeparvovec-rokl (Elevidys, Sarepta) after ...
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