Researchers created a highly efficient gene-editing method that fixes multiple DNA mutations in a single step. The breakthrough could revolutionize genetic medicine by making treatments for complex ...

Gene therapy currently represents the most promising approach for the treatment of hereditary diseases. Yet despite significant breakthroughs in recent years, there are still a number of hurdles that ...

One problem in gene therapy is that not all genes transfer equally well into the target cells. Researchers have now developed a flexible method to transfer large genes efficiently and without ...

Scientists at the University College London (UCL) have developed a novel therapy that helps treat patients with T cell acute ...

Researchers at the University of Geneva, together with colleagues in Switzerland, France, the United States and Israel, ...

The gene therapy market presents key opportunities in addressing genetic disorders by targeting the root cause through therapies like gene augmentation. North America leads in market share, with ...

CAR7, has shown remarkable success in reversing an aggressive form of leukemia. This world-first treatment uses genetically ...

Scientists looked at multiple techniques used to measure the modified viruses deployed in some gene therapy research and treatments. One technique, known as SEC-MALS, was the most precise and accurate ...

This story is part of a series on the current progression in Regenerative Medicine. In 1999, I defined regenerative medicine as the collection of interventions that restore tissues and organs damaged ...

Over the last four years, Shriners Children’s St. Louis researchers have been working to develop a new way to prevent the effects of childhood obesity. Now, using gene therapy, Shriners Children’s St.

While gene therapy for cystic fibrosis is still in the research phase, researchers aim to correct the defective gene responsible for the disease. Current research is promising. Cystic fibrosis (CF) is ...

Scientists from Kolkata-based Bose Institute have created GlowCas9--a CRISPR protein that lights up while performing gene ...